Idursulfase

Idursulfase (brand name Elaprase), manufactured by Takeda, is a drug used to treat Hunter syndrome (also called MPS-II).[1] It is a purified form of iduronate-2-sulfatase, a lysosomal enzyme, and is produced by recombinant DNA technology in a human cell line.

It is one of the most expensive drugs ever produced, costing US$567,412 per patient per year.[2][3][4]

References

  1. Preclinical dose ranging studies for enzyme replacement therapy with idursulfase in a knock-out mouse model of MPS II Mol. Genet. Metab., 2007^
  2. Drug approved to treat rare but potentially deadly disease retrieved 2011-04-29^
  3. Health Care: The World's Most Expensive Drugs, Matthew Herper, Forbes, Feb. 22, 2010^
  4. , Barbara Kollmeyer, Marketwatch, Fed. 3, 2016^